A Clinical Study to Evaluate the Efficacy and Safety of MIN-102 (IMP) in Male AMN Patients.

PHASE2/PHASE3CompletedINTERVENTIONAL
Enrollment

105

Participants

Timeline

Start Date

December 8, 2017

Primary Completion Date

June 25, 2021

Study Completion Date

March 6, 2025

Conditions
Adrenoleukodystrophy
Interventions
DRUG

MIN-102

MIN-102 treatment

DRUG

Placebos

Placebo

Trial Locations (10)

21205

Kennedy Krieger Institute, Baltimore

94304

Stanford University Medical Center, Stanford

02114

Massachusetts General Hospital, Boston

Unknown

Hospital de la Pitié-Salpêtrière, Paris

Universitat Leipzig Klinik and Poliklinik für Neurologie, Leipzig

Institute of Genomic Medicine and Rare Disorders, Budapest

Instituto Neurologico Carlo Besta, Milan

Academish Medisch Centrum, Amsterdam

Hospital Universitari Vall d'Hebrón, Barcelona

National hospital for Neurology and Neurosurgery Charles Dent Metabolic Unit), London

Sponsors
All Listed Sponsors
lead

Minoryx Therapeutics, S.L.

INDUSTRY