105
Participants
Start Date
December 8, 2017
Primary Completion Date
June 25, 2021
Study Completion Date
March 6, 2025
MIN-102
MIN-102 treatment
Placebos
Placebo
Kennedy Krieger Institute, Baltimore
Stanford University Medical Center, Stanford
Massachusetts General Hospital, Boston
Hospital de la Pitié-Salpêtrière, Paris
Universitat Leipzig Klinik and Poliklinik für Neurologie, Leipzig
Institute of Genomic Medicine and Rare Disorders, Budapest
Instituto Neurologico Carlo Besta, Milan
Academish Medisch Centrum, Amsterdam
Hospital Universitari Vall d'Hebrón, Barcelona
National hospital for Neurology and Neurosurgery Charles Dent Metabolic Unit), London
Lead Sponsor
Minoryx Therapeutics, S.L.
INDUSTRY