About
Gene Therapy
Areas of Focus
Categories
Gene Therapy, RNA & Peptide TherapyNJ, NY, PA
Clinical Trials (7)
View allTotal Trials
7
As Lead Sponsor
7
As Collaborator
0
Total Enrollment
158
By Phase
PHASE1/PHASE2: 3PHASE1: 1
By Status
RECRUITING: 3ACTIVE_NOT_RECRUITING: 2NOT_YET_RECRUITING: 1COMPLETED: 1
Clinical Trials Pipeline7 trials
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Phase 1/2
Phase 2/3
N/A
2018
2019
2020
2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
Today
Hover over trial bars to see details
Recent Trials
NCT06865482Lead Sponsor
Clinical Course Of Disease In Participants With FA-CM
N/ARecruiting
65 participants
Started: Sep 30, 2025 · Completed: Sep 30, 2027
NCT07050160Lead Sponsor
Long-term Follow-up Study of Gene Therapy for Arrhythmogenic Cardiomyopathy Due to a Plakophilin-2 Pathogenic Variant
N/ANot yet recruiting
10 participants
Started: Aug 31, 2025 · Completed: Aug 31, 2030
NCT06109181Lead Sponsor
Gene Therapy for ACM Due to a PKP2 Pathogenic Variant
PHASE1/PHASE2Recruiting
10 participants
Started: Feb 29, 2024 · Completed: Feb 28, 2027
NCT06976606Lead Sponsor
A Study to Assess Real-world Patient Characteristics and Clinical Course for Symptomatic Patients With PKP2-ACM
N/ARecruiting
40 participants
Started: Jan 23, 2024 · Completed: Sep 30, 2027
NCT05400330Lead Sponsor
Long-Term Follow-up of Gene Therapy for APOE4 Homozygote Alzheimer's Disease
PHASE1Active, not recruiting
10 participants
Started: May 8, 2023 · Completed: Nov 30, 2028
Locations (1)
Headquarters
New York, NY, United States
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