Biologics
Total Trials
3
As Lead Sponsor
As Collaborator
0
Total Enrollment
17
NCT04693598
Gene Transfer Clinical Trial for Krabbe Disease
Phase: Phase 1/2
Role: Lead Sponsor
Start: Nov 5, 2021
Completion: Nov 30, 2026
NCT05739643
Gene Transfer Clinical Trial for Infantile and Late Infantile Krabbe Disease Treated Previously With HSCT
Start: Feb 3, 2023
NCT06308718
Long-term Follow-up Study to Evaluate Safety and Efficacy of FBX-101 in Krabbe Patients
Phase: N/A
Start: Aug 6, 2024
Completion: Apr 11, 2025
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