NCT04693598 - Gene Transfer Clinical Trial for Krabbe Disease | Biotech Hunter

Enrollment

Participants

Timeline

Start Date

November 5, 2021

Primary Completion Date

November 30, 2026

Study Completion Date

November 30, 2026

Conditions

Krabbe Disease

Interventions

BIOLOGICAL

FBX-101

A replication-deficient adeno-associated virus gene transfer vector expressing the human galactocerebrosidase (GALC) cDNA will be delivered one-time through a venous catheter inserted into a peripheral limb vein.

Trial Locations (1)

48109

University of Michigan Hospitals - Michigan Medicine, Ann Arbor