Cellular & Protein-Based Therapies
Total Trials
10
As Lead Sponsor
8
As Collaborator
2
Total Enrollment
582
NCT00428935
Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy
Phase: Phase 1
Role: Collaborator
Start: Mar 31, 2006
Completion: Jul 31, 2010
NCT03533673
AAV2/8-LSPhGAA (ACTUS-101) in Late-Onset Pompe Disease
Phase: Phase 1/2
Role: Lead Sponsor
Start: Dec 17, 2018
Completion: Mar 31, 2026
NCT04179643
AB-1002 in Patients With Class III Heart Failure
Start: Nov 20, 2019
Completion: Sep 30, 2026
NCT04167540
GDNF Gene Therapy for Parkinson's Disease
Start: Apr 1, 2020
Completion: Jun 30, 2027
NCT05699460
Pre-Gene Therapy Study in Parkinson's Disease and Multiple System Atrophy
Phase: N/A
Start: Sep 29, 2022
Completion: Nov 30, 2025
NCT05230459
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)
Start: May 15, 2023
Completion: Dec 31, 2028
NCT05598333
Phosphatase Inhibition by Intracoronary Gene Therapy in Subjects With Non-Ischemic NYHA Class III Heart Failure
Phase: Phase 2
Start: Oct 20, 2023
Completion: Dec 31, 2030
NCT06285643
A Study of AAV2-GDNF in Adults With Moderate Parkinson's Disease (REGENERATE-PD)
Start: Jun 11, 2024
Completion: Nov 30, 2027
NCT07081841
AB-1005 Long-Term Follow-up Study
Start: Sep 4, 2025
Completion: Mar 30, 2038
NCT07215403
Prescriptive Infusion Algorithm (PIA)
Start: May 1, 2026
Completion: Mar 1, 2028
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