Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy

PHASE1CompletedINTERVENTIONAL
Enrollment

6

Participants

Timeline

Start Date

March 31, 2006

Primary Completion Date

March 31, 2009

Study Completion Date

July 31, 2010

Conditions
Duchenne Muscular Dystrophy
Interventions
BIOLOGICAL

rAAV2.5-CMV-minidystrophin (d3990)

Recombinant adeno-associated virus (AAV) carrying a truncated human dystrophin gene (mini-dystrophin) expressed from a cytomegalovirus (CMV) promoter.

Trial Locations (1)

43205

Columbus Children's Hospital, Columbus

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

AskBio Inc

INDUSTRY

lead

Nationwide Children's Hospital

OTHER

NCT00428935 - Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy | Biotech Hunter | Biotech Hunter