6
Participants
Start Date
March 31, 2006
Primary Completion Date
March 31, 2009
Study Completion Date
July 31, 2010
rAAV2.5-CMV-minidystrophin (d3990)
Recombinant adeno-associated virus (AAV) carrying a truncated human dystrophin gene (mini-dystrophin) expressed from a cytomegalovirus (CMV) promoter.
Columbus Children's Hospital, Columbus
Collaborators (1)
AskBio Inc
INDUSTRY
Nationwide Children's Hospital
OTHER