Mutated exon replacement
Total Trials
2
As Lead Sponsor
As Collaborator
0
Total Enrollment
63
NCT06467344
Study to Evaluate ACDN-01 in ABCA4-related Stargardt Retinopathy (STELLAR)
Phase: Phase 1/2
Role: Lead Sponsor
Start: Jun 11, 2024
Completion: Dec 1, 2030
NCT06445322
Prescreening Study to Identify Potential Stargardt Participants for ACDN-01 Clinical Trials
Phase: N/A
Start: Jun 20, 2024
Completion: Aug 31, 2030
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