13
Participants
Start Date
June 11, 2024
Primary Completion Date
August 1, 2030
Study Completion Date
December 1, 2030
ACDN-01
ACDN-01 is an AAV-based vector carrying a DNA construct encoding for an ABCA4 RNA exon editor. One time administration is via subretinal injection.
RECRUITING
Wilmer Eye Institute at John Hopkins, Baltimore
RECRUITING
Vitreo Retinal Associates, Gainesville
RECRUITING
Bascom Palmer Eye Institute, Miami
RECRUITING
Cincinnati Eye Institute, Cincinnati
RECRUITING
University of Michigan Kellogg Eye Center, Ann Arbor
RECRUITING
Retina Foundation of the Southwest, Dallas
RECRUITING
Retina Consultants of Texas, Houston
RECRUITING
University of San Francisco, San Francisco
RECRUITING
Casey Eye Institute OHSU, Portland
RECRUITING
Massachusetts Eye and Ear, Boston
Lead Sponsor
Ascidian Therapeutics, Inc
INDUSTRY