Study to Evaluate ACDN-01 in ABCA4-related Stargardt Retinopathy (STELLAR)

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

13

Participants

Timeline

Start Date

June 11, 2024

Primary Completion Date

August 1, 2030

Study Completion Date

December 1, 2030

Conditions
Stargardt DiseaseCone Rod DystrophyJuvenile Macular DegenerationStargardt Disease 1
Interventions
DRUG

ACDN-01

ACDN-01 is an AAV-based vector carrying a DNA construct encoding for an ABCA4 RNA exon editor. One time administration is via subretinal injection.

Trial Locations (10)

21218

RECRUITING

Wilmer Eye Institute at John Hopkins, Baltimore

32607

RECRUITING

Vitreo Retinal Associates, Gainesville

33136

RECRUITING

Bascom Palmer Eye Institute, Miami

45245

RECRUITING

Cincinnati Eye Institute, Cincinnati

48105

RECRUITING

University of Michigan Kellogg Eye Center, Ann Arbor

75382

RECRUITING

Retina Foundation of the Southwest, Dallas

77401

RECRUITING

Retina Consultants of Texas, Houston

94158

RECRUITING

University of San Francisco, San Francisco

97239

RECRUITING

Casey Eye Institute OHSU, Portland

02114

RECRUITING

Massachusetts Eye and Ear, Boston

Sponsors
All Listed Sponsors
lead

Ascidian Therapeutics, Inc

INDUSTRY

NCT06467344 - Study to Evaluate ACDN-01 in ABCA4-related Stargardt Retinopathy (STELLAR) | Biotech Hunter | Biotech Hunter