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Clinical Trials for Zevra Therapeutics
Explore 2 clinical trials worldwide
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Showing 1-2 of 2 trials
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Status: Recruiting, Active, not recruiting, Enrolling by invitation, Not yet recruiting
Sponsor: Zevra Therapeutics
Clinical Trials (2)
NCT07125066
An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2 Hydroxyglutaric Aciduria (C-2HGA)
PHASE1
Enrolling by invitation
1 participants
Started: Jul 30, 2025 · Completed: Dec 31, 2027
1 condition
2 sponsors
1 location
NCT06773026
Study of Sodium Phenylbutyrate (ACER-001) for the Treatment of Pediatric and Adults Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD)
PHASE2
Recruiting
24 participants
Started: Jun 30, 2025 · Completed: Jul 31, 2027
1 condition
2 sponsors
1 location