Clinical Trials for Orchard Therapeutics

Explore 8 clinical trials worldwide

Showing 1-8 of 8 trials

Active filters:Status: Recruiting, Active, not recruiting, Enrolling by invitation, Not yet recruitingSponsor: Orchard Therapeutics

Clinical Trials (8)

A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCT

PHASE3Active, not recruiting

41 participants

Started: Dec 11, 2023 · Completed: Mar 31, 2031

1 condition1 sponsor5 locations

OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)

PHASE3Active, not recruiting

Started: Jan 17, 2022 · Completed: Mar 31, 2031

2 conditions2 sponsors1 location

ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program

N/AEnrolling by invitation

100,000 participants

Started: May 10, 2021 · Completed: Aug 31, 2029

14 conditions19 sponsors9 locations

Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type IIIA

PHASE1/PHASE2Active, not recruiting

Started: Jan 7, 2020 · Completed: Oct 30, 2026

1 condition6 sponsors1 location

Gene Therapy With Modified Autologous Hematopoietic Stem Cells for the Treatment of Patients With Mucopolysaccharidosis Type I, Hurler Variant

PHASE1/PHASE2Active, not recruiting

Started: May 11, 2018 · Completed: Mar 31, 2028

1 condition2 sponsors1 location

A Safety and Efficacy Study of Cryopreserved OTL-200 for Treatment of Metachromatic Leukodystrophy (MLD)

PHASE2Active, not recruiting

10 participants

Started: Jan 25, 2018 · Completed: Jan 31, 2026

2 conditions2 sponsors1 location

The Myelin Disorders Biorepository Project

12,000 participants

Started: Dec 8, 2016 · Completed: Dec 8, 2030

66 conditions21 sponsors23 locations

Gene Therapy for Metachromatic Leukodystrophy (MLD)

PHASE1/PHASE2Active, not recruiting

20 participants

Started: Apr 9, 2010 · Completed: Sep 19, 2025

2 conditions2 sponsors1 location