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Clinical Trials for Mahzi Therapeutics
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Status: Recruiting, Active, not recruiting, Enrolling by invitation, Not yet recruiting
Sponsor: Mahzi Therapeutics
Clinical Trials (1)
NCT07135050
Phase 1/2 Study of MZ-1866, an AAV-9 Gene Therapy Delivered by Intracerebroventricular Injection to Participants With Pitt Hopkins Syndrome
PHASE1/PHASE2
Not yet recruiting
12 participants
Started: Jan 31, 2026 · Completed: Jul 31, 2029
1 condition
1 sponsor
0 locations