Clinical Trials for GEMMA Biotherapeutics

Explore 2 clinical trials worldwide

Showing 1-2 of 2 trials

Active filters:Status: Recruiting, Active, not recruiting, Enrolling by invitation, Not yet recruitingSponsor: GEMMA Biotherapeutics

Clinical Trials (2)

NCT07070999
Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1
PHASE1/PHASE2Not yet recruiting
22 participants
Started: Oct 31, 2025 · Completed: Apr 30, 2029
1 condition1 sponsor0 locations
NCT04713475
Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis
PHASE1/PHASE2Active, not recruiting
26 participants
Started: Mar 17, 2021 · Completed: Feb 28, 2029
4 conditions1 sponsor7 locations