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Clinical Trials for BlackfinBio
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Status: Recruiting, Active, not recruiting, Enrolling by invitation, Not yet recruiting
Sponsor: BlackfinBio
Clinical Trials (1)
NCT06948019
Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47)
PHASE1/PHASE2
Not yet recruiting
5 participants
Started: Aug 31, 2025 · Completed: Aug 31, 2032
13 conditions
2 sponsors
1 location