Decoding Central Defects in Dystrophinopathies From Diagnostic to Remediation

Not yet recruitingOBSERVATIONAL
Enrollment

110

Participants

Timeline

Start Date

October 1, 2025

Primary Completion Date

October 1, 2027

Study Completion Date

April 1, 2029

Conditions
Dystrophinopathies
Trial Locations (1)

75015

Hôpital Necker Enfants Malades, Paris

All Listed Sponsors
lead

Assistance Publique - Hôpitaux de Paris

OTHER

NCT07125898 - Decoding Central Defects in Dystrophinopathies From Diagnostic to Remediation | Biotech Hunter | Biotech Hunter