Global Open-Label Extension Study of Del-desiran for the Treatment of DM1

PHASE3Enrolling by invitationINTERVENTIONAL
Enrollment

217

Participants

Timeline

Start Date

July 25, 2025

Primary Completion Date

August 31, 2030

Study Completion Date

October 31, 2030

Conditions
Myotonic Dystrophy Type 1DM1Myotonic DystrophyMyotoniaMyotonic Dystrophy 1Myotonic DisordersSteinert Myotonic DystrophySteinert's Disease
Interventions
DRUG

Del-desiran (AOC 1001)

Del-desiran will be administered by intravenous (IV) infusion.

Trial Locations (9)

14642

University of Rochester Medical Center, Rochester

23298

Virginia Commonwealth University, Richmond

32608

University of Florida, Gainesville

43221

Ohio State University, Columbus

66205

Kansas University Medical Center, Kansas City

77030

Houston Methodist Neurological Institute, Houston

80045

University of Colorado, Denver

90095

University of California, Los Angeles (UCLA), Los Angeles

94305

Stanford University, Stanford

Sponsors
All Listed Sponsors
lead

Avidity Biosciences, Inc.

INDUSTRY

NCT07008469 - Global Open-Label Extension Study of Del-desiran for the Treatment of DM1 | Biotech Hunter | Biotech Hunter