Phase 4 Study: Long-term Safety and Efficacy of NT-501 in MacTel Type 2, Including Sham Procedure Participants

PHASE4Not yet recruitingINTERVENTIONAL
Enrollment

285

Participants

Timeline

Start Date

August 15, 2025

Primary Completion Date

August 15, 2030

Study Completion Date

August 15, 2030

Conditions
Macular Telangiectasia Type 2 (MacTel)
Interventions
COMBINATION_PRODUCT

NT-501/revakinagene taroretcel-lwey

NT-501 is surgically implanted into the vitreous cavity to continuously release recombinant human ciliary neurotrophic factor (CNTF).

Trial Locations (33)

19104

Scheie Eye Institute, Philadelphia

20892

National Eye Institute, Bethesda

21237

Elman Retina Group, PA, Baltimore

21702

Cumberland Valley Retina Consultants, Frederick

30322

Emory Eye Center, Atlanta

37922

Southeastern Retina Associates, P.C., Knoxville

44126

Retina Associates of Cleveland, Inc., Cleveland

45242

Cincinnati Eye Institute, Cincinnati

49525

Foundation for Vision Research, Grand Rapids

53705

University of Wisconsin, Madison

55905

Mayo Clinic, Rochester

60611

Northwestern University, Chicago

63144

The Retina Institute, St Louis

74132

Tulsa Retina Consultants, Tulsa

75231

Texas Retina Associates, Dallas

75251

Retina Center of Texas, Dallas

77030

Retina Consultants of Texas, Houston

84132

University of Utah John A. Moran Center, Salt Lake City

90085

Jules Stein Eye Institute/UCLA, Los Angeles

92037

Scripps Health, La Jolla

94303

Stanford University School of Medicine, Palo Alto

94598

Bay Area Retina Associates, Walnut Creek

97221

Retina Northwest, P.C., Portland

02114

Massachusetts Eye and Ear Infirmary, Retina Service, Boston

07003

Envision Ocular, LLC, Bloomfield

Unknown

Cerulea, East Melbourne

Lion's Eye Institute, Perth

Sydney Eye Hospital, Sydney

Lariboisiére Hospital, Paris

University Eye Hospital Bonn, Bonn

UNIVERSITÄTSKLINIKUM FREIBURG, Klinik für Augenheilkunde, Freiburg im Breisgau

Augenzentrum am St. Franziskus-Hospital, Münster

Oxford University Hospitals NHS FT, Oxford

Sponsors
All Listed Sponsors
lead

Neurotech Pharmaceuticals

INDUSTRY