Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease

RecruitingOBSERVATIONAL
Enrollment

480

Participants

Timeline

Start Date

June 1, 2024

Primary Completion Date

October 1, 2030

Study Completion Date

October 1, 2030

Conditions
Sickle Cell Disease (SCD)
Trial Locations (37)

10032

NOT_YET_RECRUITING

Columbia Presbytarian (NT-DMT), New York

10467

NOT_YET_RECRUITING

Children's Hospital at Montefiore (MRD HCT), The Bronx

RECRUITING

Children's Hospital at Montefiore (NT-DMT), The Bronx

11040

NOT_YET_RECRUITING

Cohen's Children Hospital (NT-DMT), Queens

14203

RECRUITING

Roswell Park (MRD-HCT), Buffalo

14642

NOT_YET_RECRUITING

University of Rochester (MRD-HCT), Rochester

NOT_YET_RECRUITING

University of Rochester (NT-DMT), Rochester

19104

RECRUITING

Children's Hospital of Philadelphia (MRD-HCT), Philadelphia

19803

RECRUITING

Nemours Children's Hospital, Delaware (MRD-HCT), Wilmington

20010

RECRUITING

Children's National Hospital (MRD-HCT), Washington D.C.

27514

NOT_YET_RECRUITING

UNC Children's Hospital (MRD HCT), Chapel Hill

28203

RECRUITING

Atrium Health (MRD-HCT), Charlotte

30329

RECRUITING

Children's Healthcare of Atlanta (MRD-HCT), Atlanta

35294

RECRUITING

Children's of Alabama (MRD-HCT), Birmingham

NOT_YET_RECRUITING

Children's of Alabama (NT-DMT), Birmingham

38105

NOT_YET_RECRUITING

St Jude Children Hospital (NT-DMT), Memphis

RECRUITING

St. Jude Children's Research Hospital (MRD-HCT), Memphis

43205

NOT_YET_RECRUITING

Nationwide Children's Hospital (NT-DMT), Columbus

46202

RECRUITING

Riley Children's Hospital (MRD-HCT), Indianapolis

NOT_YET_RECRUITING

Riley's Children Hospital (NT-DMT), Indianapolis

60637

RECRUITING

Comer Children's Hospital (MRD-HCT), Chicago

63130

NOT_YET_RECRUITING

Wahington Univ in St Louis (NT-DMT), St Louis

NOT_YET_RECRUITING

Washington University in St Louis (MRD-HCT), St Louis

73104

NOT_YET_RECRUITING

Oklahoma Children's Hospital (MRD-HCT), Oklahoma City

77030

NOT_YET_RECRUITING

Texas Children's Hopsital (NT-DMT), Houston

RECRUITING

Texas Children's Hospital (MRD-HCT), Houston

78229

NOT_YET_RECRUITING

UT San Antonio (NT-DMT), San Antonio

02115

RECRUITING

Boston Children's Hospital (MRD-HCT), Boston

NOT_YET_RECRUITING

Boston Children's Hospital (NT-DMT), Boston

07601

RECRUITING

Hackensack University Hospital (MRD-HCT), Hackensack

27599.

NOT_YET_RECRUITING

UNC Children's Hospital (NT-DMT), Chapel Hill

T3B 6A8

NOT_YET_RECRUITING

Alberta Children's Hospital (NT-DMT), Calgary

T3B6A8

RECRUITING

Alberta Children's Hospital (MRD-HCT), Calgary

Unknown

NOT_YET_RECRUITING

British Columbia Children's Hosptial (MRD HCT), Vancouver

NOT_YET_RECRUITING

Universite de Montreal / Ste Justine (MRD HCT), Montreal

R3E 0V9

RECRUITING

HSC Winnipeg Children's Hospital/University of Manitoba (MRD-HCT), Winnipeg

ON M5G 1E8

NOT_YET_RECRUITING

The Hospital for Sick Children (MRD-HCT), Toronto

All Listed Sponsors
collaborator

Patient-Centered Outcomes Research Institute

OTHER

lead

University of Rochester

OTHER