Preparation of IPSC for Cell Gene Editing for the Treatment of AATD

NAEnrolling by invitationINTERVENTIONAL

Enrollment

Participants

Timeline

Start Date

January 15, 2025

Primary Completion Date

February 28, 2026

Study Completion Date

February 28, 2026

Conditions

Alpha1-antitrypsin Deficiency

Interventions

GENETIC

iPSC generation

Base editing

Trial Locations (1)

Fondazione IRCCS Policlinico San Matteo, Sc Pneumologia, Pavia

All Listed Sponsors

collaborator

University of Bern

OTHER

lead

Fondazione IRCCS Policlinico San Matteo di Pavia

OTHER