An Observational Study of Participants With Type 3 Von Willebrand Disease on Prophylactic Standard-of-Care Treatment

RecruitingOBSERVATIONAL
Enrollment

40

Participants

Timeline

Start Date

April 29, 2025

Primary Completion Date

November 1, 2026

Study Completion Date

November 1, 2026

Conditions
Von Willebrand Disease, Type 3
Interventions
DRUG

Von Willebrand Factor Concentrates

Used according to local labeling or local treatment guidelines.

DRUG

Von Willebrand Factor Concentrates and Factor VIII Concentrates

Used according to local labeling or local treatment guidelines.

DRUG

Factor VIII Concentrates

Used according to local labeling or local treatment guidelines.

DRUG

Recombinant Activated Factor VII

Used according to local labeling or local treatment guidelines.

DRUG

Activated Prothrombin Complex Concentrate

Used according to local labeling or local treatment guidelines.

Trial Locations (23)

3000

RECRUITING

UZ Leuven Gasthuisberg, Leuven

28046

RECRUITING

Hospital Universitario la Paz, Madrid

41013

RECRUITING

Hospital Universtiario Virgen del Rocio, Seville

47051

RECRUITING

Gerinnungszentrum Rhein-Ruhr;Gerinnungsambulanz, Duisburg

50134

RECRUITING

AOU Careggi, Florence

53127

RECRUITING

Universitätsklinikum Bonn, Bonn

59037

RECRUITING

Hopital Claude Huriez - CHU Lille, Lille

60590

RECRUITING

Hämophiliezentrum Med. Klinik III/Institut für Transfusionsmedizin, Frankfurt/M.

63110

RECRUITING

Washington University School of Medicine, St Louis

75015

RECRUITING

Groupe Hospitalier Necker Enfants Malades, Paris

95817

RECRUITING

UC Davis, Sacramento

M5G 1X8

RECRUITING

The Hospital for Sick Children, Toronto

H4A 3J1

RECRUITING

McGill University Health Center, Montreal

Unknown

RECRUITING

IPS SURA Industriales Medellín, Medellín

00161

RECRUITING

Universita' Degli Studi La Sapienza-Ist.Di Ematologia, Rome

830-0011

RECRUITING

Kurume University Hospital, Fukuoka

160-0023

RECRUITING

Tokyo Medical University Hospital, Tokyo

3015 GD

RECRUITING

Erasmus MC, Rotterdam

02-776

RECRUITING

Instytut Hematologii i Transfuzjologii, Warsaw

S-413 45

RECRUITING

Sahlgrenska Universitetssjukhuset, Gothenburg

SE1 7EH

RECRUITING

St Thomas' Hospital, London

WC1N 3JH

RECRUITING

Great Ormond Street Hospital, London

M13 9WL

RECRUITING

Manchester Royal Infirmary, Manchester

All Listed Sponsors
lead

Hoffmann-La Roche

INDUSTRY