200
Participants
Start Date
May 31, 2025
Primary Completion Date
March 1, 2029
Study Completion Date
March 1, 2029
Blood sampling for dosage
4ml blood sample to measure acid sphingomyelinase enzyme activity and LysoSM, if required.
Groupe Hospitalier Diaconesses Croix Saint-Simon, Paris
Bichat Hospital
OTHER
Hospital Avicenne
OTHER
Rennes University Hospital
OTHER
Bicetre Hospital
OTHER
University Hospital, Marseille
OTHER
Tenon Hospital, Paris
OTHER
Centre Hospitalier Universitaire Dijon
OTHER
University Hospital, Lille
OTHER
Hospices Civils de Lyon
OTHER
Wladimir MAUHIN, Dr
OTHER