Italian NCL Registry: a Registry for NCL as an Integration Tool for Future Therapeutic Strategies

RecruitingOBSERVATIONAL
Enrollment

50

Participants

Timeline

Start Date

July 19, 2024

Primary Completion Date

July 19, 2026

Study Completion Date

July 19, 2027

Conditions
Neuronal Ceroid Lipofuscinosis
Trial Locations (1)

56128

RECRUITING

IRCCS Fondazione Stella Maris, Pisa

All Listed Sponsors
collaborator

Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta

OTHER

collaborator

Bambino Gesù Hospital and Research Institute

OTHER

lead

IRCCS Fondazione Stella Maris

OTHER