NCT06795152 - Rare Glycogen Storage Diseases Natural History Study | Biotech Hunter

Enrollment

200

Participants

Timeline

Start Date

December 23, 2024

Primary Completion Date

December 31, 2034

Study Completion Date

December 31, 2034

Conditions

Glycogen Storage DiseaseGSD Type 0AGSD Type 0BGSD VIITarui DiseaseGSD XGSD XIIGSD XIIIGSD XVPGBM2PRKAG2Danon DiseasePolyglucosan Body Myopathy Type 1Polyglucosan Body Myopathy Type 2RBCK1 Deficiency

Interventions

OTHER

No intervention

Observational. Natural history study.

Trial Locations (1)

27710

RECRUITING

Duke University, Durham