408
Participants
Start Date
February 17, 2025
Primary Completion Date
August 27, 2027
Study Completion Date
April 27, 2029
Etavopivat
Etavopivat will be administered orally.
Placebo
Placebo matching Etavopivat will be administered orally.
WITHDRAWN
The Royal Hospital, Muscat
RECRUITING
Sultan Qaboos University Hospital, Muscat
NOT_YET_RECRUITING
Kintampo Health Research Centre (KHRC), Kintampo, Ghana, Kintampo
NOT_YET_RECRUITING
CHU Saint-Pierre - UMC Sint-Pieter, Brussels
NOT_YET_RECRUITING
CHU - UVC Brugmann, Brussels
NOT_YET_RECRUITING
HUB - Hôpital Erasme, Brussels
NOT_YET_RECRUITING
Hospital Nini, Tripoli
RECRUITING
Prince of Wales Hospital - Department of Haematology, Randwick
RECRUITING
Royal Prince Alfred Hospital, Camperdown
NOT_YET_RECRUITING
UZ Antwerpen - UZA - Haematology, Edegem
NOT_YET_RECRUITING
UZ Antwerpen - UZA - Kinderhemato-Oncologie, Edegem
NOT_YET_RECRUITING
UZ Leuven - Kindergeneeskunde, Leuven
RECRUITING
Monash Health, Clayton
NOT_YET_RECRUITING
Sociedad de Oncología y Hematología del Cesar SAS (SOHEC), Antioquia
RECRUITING
Fiona Stanley Hospital - Haemophilia and Haemostasis Centre, Murdoch
NOT_YET_RECRUITING
Joint Clinical Research Centre (JCRC), Kampala
NOT_YET_RECRUITING
Azienda Ospedaliera Universitaria San Luigi Gonzaga - S.C.D.O. Microcitemie e malattie rare ematologiche, Orbassano
NOT_YET_RECRUITING
Azienda Ospedaliera Universitaria San Luigi Gonzaga, Orbassano
RECRUITING
Jacobi Medical Center, The Bronx
RECRUITING
Montefiore Medical Ctr, The Bronx
NOT_YET_RECRUITING
Northwell Health, Mount Kisco
RECRUITING
Cohen Children's Medical Ctr, Queens
RECRUITING
NYC Health+Hospitals, Brooklyn
RECRUITING
Interfaith Medical Center, Brooklyn
NOT_YET_RECRUITING
Hippokration Hospital, Athens
RECRUITING
King Faisal Specialist Hospital & Research Centre, Riyadh, Riyadh
RECRUITING
Children's Hosptl Philadelphia, Philadelphia
RECRUITING
St Christopher Hosp for Child, Philadelphia
RECRUITING
Nemours/AI duPont Hosp-Chld, Wilmington
NOT_YET_RECRUITING
Childrens National Medical Ctr, Washington D.C.
RECRUITING
MedStar Hlth Res Institute, Washington D.C.
NOT_YET_RECRUITING
Fondazione IRCCS San Gerardo dei Tintori, Monza
RECRUITING
Inova Health System, Fairfax
RECRUITING
Virginia Comm Univ Medical Ctr, Richmond
RECRUITING
Children's Hsptl Of The Kings, Norfolk
NOT_YET_RECRUITING
ASST Civili di Brescia, Brescia
RECRUITING
Atrium Health-Wake Forest Bapt, Winston-Salem
RECRUITING
Duke Comprehen Sickle Cell, Durham
RECRUITING
Duke University Medical Center, Durham
RECRUITING
East Carolina Univ-Greenville, Greenville
NOT_YET_RECRUITING
Hospital Gregorio Marañón, Madrid
NOT_YET_RECRUITING
Hospital Universitario La Paz, Madrid
RECRUITING
Children's Healthcare Atlanta, Atlanta
NOT_YET_RECRUITING
Centre Hospitalier Universitaire de Bordeaux-Hopital Pellegrin, Bordeaux
RECRUITING
Memorial Healthcare, Hollywood
RECRUITING
Mersin University Medical Faculty Pediatric Hematology, Mersin
NOT_YET_RECRUITING
Mersin University Medical Faculty Pediatric Hematology, Mersin
RECRUITING
VM Medical Park Mersin Hospital, Mersin
RECRUITING
National Guard Hospital Dammam, Dhahran
NOT_YET_RECRUITING
Azienda Ospedale Universita Padova, Padua
RECRUITING
Uni of Alabama at Birmingham, Birmingham
RECRUITING
King Abdulaziz Hospital-Al Ahsa-National Guard, Al Ahsa
RECRUITING
Univer South Alabama Ped/Onc, Mobile
NOT_YET_RECRUITING
Azienda Ospedaliera Universitaria Integrata Verona Policlinico GB Rossi - Borgo Roma, Verona
NOT_YET_RECRUITING
Centre Hospitalier Universitaire Grenoble Alpes-Site Nord Michallon-1, Grenoble
NOT_YET_RECRUITING
Methodist University Hospital, Memphis
NOT_YET_RECRUITING
St. Jude Children's Res Hosp, Memphis
NOT_YET_RECRUITING
Ahero Clinical Trials Unit, Kisumu, Kenya, Kisumu
NOT_YET_RECRUITING
Hospital Universitario Virgen del Rocío, Seville
NOT_YET_RECRUITING
Azienda Ospedaliero Universitaria Di Modena - UOC Pediatria ad indirizzo Oncoematologico, Modena
RECRUITING
Ohio State Univ Wexner Med Ctr, Columbus
RECRUITING
Univ Hosp Cleveland Med Ctr, Cleveland
NOT_YET_RECRUITING
University General Hospital Of Ioannina, Ioannina
WITHDRAWN
Henry Ford Hospital_Detroit, Detroit
NOT_YET_RECRUITING
Hospital Pablo Tobon Uribe, Medellín
RECRUITING
University of Minnesota, Minneapolis
RECRUITING
Childrens Hospital of Chicago, Chicago
NOT_YET_RECRUITING
Univer Of Illinois at Chicago, Chicago
RECRUITING
Washington University-St.Louis, St Louis
RECRUITING
Children's Nebraska, Omaha
NOT_YET_RECRUITING
Hospices Civils de Lyon-Hopital Edouard Herriot, Lyon
RECRUITING
Children's Hosp-New Orleans, New Orleans
RECRUITING
Arkansas Children's Hospital, Little Rock
RECRUITING
Univ of OK Health Sciences Ctr, Oklahoma City
NOT_YET_RECRUITING
Ap-Hp-Hopital Necker-1, Paris
NOT_YET_RECRUITING
Ap-Hp-Hopital Robert Debre, Paris
NOT_YET_RECRUITING
Centre Hospitalier Universitaire de Rouen-Hopital Charles Nicolle, Rouen
RECRUITING
UT Health University of Texas, Houston
NOT_YET_RECRUITING
Clinica de la Costa, Barranquilla
WITHDRAWN
Clinical and Transl Res Center, Aurora
NOT_YET_RECRUITING
"A.O.U. Università Studi della Campania Luigi Vanvitelli", Naples
RECRUITING
Phoenix Children's Hsptl, Phoenix
WITHDRAWN
Cure 4 the Kids Foundation, Las Vegas
RECRUITING
Children's Hospital Los Angeles - Endocrinology, Los Angeles
RECRUITING
UCLA Health, Los Angeles
NOT_YET_RECRUITING
Azienda Ospedaliera Ospedali Riuniti Villa Sofia - Cervello, Palermo
RECRUITING
Harbor-UCLA Medical Center, Torrance
WITHDRAWN
University Of California Irvine, Orange
NOT_YET_RECRUITING
Ap-Hp-Hopital Avicenne, Bobigny
RECRUITING
Valley Children's Hospital, Madera
NOT_YET_RECRUITING
Ap-Hp-Hopital Henri Mondor, Créteil
RECRUITING
Stanford University_Palo Alto, Palo Alto
NOT_YET_RECRUITING
ARNAS Garibaldi Catania - Presidio Ospedaliero Garibaldi-Centro, Catania
RECRUITING
Mary Bridge Children's Health, Tacoma
NOT_YET_RECRUITING
Mary Bridge Children's Health, Tacoma
NOT_YET_RECRUITING
Lagos University Teaching Hospital, Lagos, Lagos
RECRUITING
All India Institute of Medical Sciences_New Dehli, New Delhi
NOT_YET_RECRUITING
Sociedad de Oncología y Hematología del Cesar SAS (SOHEC), Valledupar
RECRUITING
Post Graduate Institute of Child Health, Noida
NOT_YET_RECRUITING
Clínica IMAT Oncomedica Auna S.A.S., Montería
NOT_YET_RECRUITING
Clínica IMAT Oncomedica Auna S.A.S., Montería
NOT_YET_RECRUITING
RNT Medical College, Udaipur
RECRUITING
Zydus Medical College & Hospital, Dohad
RECRUITING
SSG Hospital, Baroda, Vadodara
RECRUITING
HOCC Haemato Oncology Care Centre, Vadodara
RECRUITING
Nirmal Hospital Pvt. Ltd., Surat
RECRUITING
Arihant Multispeciality Hospital, Nagpur
RECRUITING
All India Institute of Medical Sciences (AIIMS), Raipur, Raipur
NOT_YET_RECRUITING
NIZAM'S Institute of Medical Sciences, Hyderabad
RECRUITING
JSS Hospital, Mysore, Mysuru
RECRUITING
Government Medical College, Kozhikode, Kozhikode
NOT_YET_RECRUITING
Government Medical College, Kozhikode, Kozhikode
RECRUITING
IMS and SUM Hospital, Bhubaneswar
NOT_YET_RECRUITING
Centro de investigaciones clínicas, fudación valle del lili, Santiago de Cali
NOT_YET_RECRUITING
Centro de investigaciones clínicas, fudación valle del lili, Santiago de Cali
RECRUITING
Gauhati Medical College and Hospital, Guwahati
NOT_YET_RECRUITING
Boston Children's Hospital, Boston
RECRUITING
Boston Medical Center, Boston
NOT_YET_RECRUITING
Newark Beth Israel Medical Center, Newark
NOT_YET_RECRUITING
MultiHemo - Grupo Oncoclínicas, Recife
NOT_YET_RECRUITING
MultiHemo - Grupo Oncoclínicas, Recife
RECRUITING
Hemocentro UNICAMP, Distrito de Barão Geraldo - Campinas
RECRUITING
HC da FMUSP Hospital das Clínicas São Paulo, São Paulo
NOT_YET_RECRUITING
HC da FMUSP Hospital das Clínicas São Paulo, São Paulo
RECRUITING
Fundação Hemocentro de Ribeirão Preto, Ribeirão Preto
RECRUITING
Hemorio-Fundarj, Rio de Janeiro
RECRUITING
Hospital Samaritano Higienópolis - Instituto de Conhecimento Ensino e Pesquisa (ICEP), São Paulo
RECRUITING
Foothills Med Ctr-Univ Calgary, Calgary
NOT_YET_RECRUITING
Stollery Children's Hospital, Edmonton
NOT_YET_RECRUITING
University of Alberta_Edmonton, Edmonton
NOT_YET_RECRUITING
BC Children's Hospital, Vancouver
RECRUITING
LHSC - Victoria Hospital, London
WITHDRAWN
UHN-Toronto General Hospital, Toronto
NOT_YET_RECRUITING
University of Toronto, Toronto
NOT_YET_RECRUITING
CHUM-Hosp de Univ Montreal, Montreal
NOT_YET_RECRUITING
Montreal Children's Hospital, Montreal
WITHDRAWN
Agogo Presbyterian Hospital, Ghana, Agogo
NOT_YET_RECRUITING
KEMRI Siaya Clinical Research Annex Siaya County Referral Hospital, Siaya, Siaya
NOT_YET_RECRUITING
International Cancer Institute (ICI), Uasin Gishu County
NOT_YET_RECRUITING
University College Hospital Paediatric Haematology and Oncology Unit, Ibadan, Ibadan
NOT_YET_RECRUITING
Centre for Sickle Cell Disease Research and Training University of Abuja (CESRTA), Abuja, Abuja
NOT_YET_RECRUITING
Jinja Regional Referral Hospital Children's Ward, Jinja
NOT_YET_RECRUITING
Makerere University College of Health Sciences, Kampala
NOT_YET_RECRUITING
Navrongo Health Research Centre, Ghana, Navrongo
NOT_YET_RECRUITING
Gertrude's Children's Hospital, Nairobi, Nairobi
NOT_YET_RECRUITING
University of Nigeria Teaching Hospital, Enugu, Enugu
NOT_YET_RECRUITING
"Laiko General Hospital of Athens", Athens
NOT_YET_RECRUITING
"Childrens' Hospital of Athens Agia Sofia", Athens
NOT_YET_RECRUITING
"AHEPA University General Hospital of Thessaloniki", Thessaloniki
NOT_YET_RECRUITING
American University of Beirut Medical Centre, Hamra
NOT_YET_RECRUITING
Amsterdam UMC Lokatie VUMC, Amsterdam
NOT_YET_RECRUITING
Erasmus MC, Rotterdam
NOT_YET_RECRUITING
Haga Ziekenhuis, The Hague
NOT_YET_RECRUITING
UMC Utrecht, Van Creveldkliniek, Utrecht
NOT_YET_RECRUITING
Hospital Vall d'Hebron, Barcelona
RECRUITING
Acibadem Adana Hastanesi, Adana
RECRUITING
Baskent Universitesi Adana, Adana
RECRUITING
Cukurova University Medical Faculty, Adana
RECRUITING
Hacettepe University Hematology, Ankara
NOT_YET_RECRUITING
Addenbrooke's Hospital, Cambridge
RECRUITING
Whittington Hospital, London
NOT_YET_RECRUITING
Guy's Hospital, London
NOT_YET_RECRUITING
King's College Hospital - Paediatric Research, London
RECRUITING
Kings College Hospital, London
RECRUITING
Imperial College London, London
Lead Sponsor
Novo Nordisk A/S
INDUSTRY