A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

PHASE3RecruitingINTERVENTIONAL
Enrollment

480

Participants

Timeline

Start Date

January 10, 2025

Primary Completion Date

December 30, 2030

Study Completion Date

December 30, 2030

Conditions
Sickle Cell DiseaseThalassemia
Interventions
DRUG

Etavopivat A

Participants will receive an oral dose of Etavopivat A.

DRUG

Etavopivat B

Participants will receive an oral dose of Etavopivat B.

DRUG

Etavopivat C

Participants will receive an oral dose of Etavopivat C.

Trial Locations (100)

0

NOT_YET_RECRUITING

Faculty of Medicine Ain Shams Medical Research Institute (MASRI), Cairo

NOT_YET_RECRUITING

Ghana Institute of Clinical Genetics, Korle Bu Teaching Hospital (KBTH), Accra

123

RECRUITING

Sultan Qaboos University Hospital, Muscat

200

NOT_YET_RECRUITING

Kintampo Health Research Centre (KHRC), Kintampo, Ghana, Kintampo

228

NOT_YET_RECRUITING

University of Abuja Teaching Hospital, Gwagwalada, Abuja, Abuja

1434

RECRUITING

Hospital Nini, Tripoli

1932

NOT_YET_RECRUITING

Kombewa Clinical Research Centre, Kisumu

3452

NOT_YET_RECRUITING

Aminu Kano Teaching Hospital (AKTH), Kano

10032

RECRUITING

Columbia University Medical Center_New York_0, New York

NOT_YET_RECRUITING

Columbia University Medical Center_New York_0, New York

10043

RECRUITING

Azienda Ospedaliera Universitaria San Luigi Gonzaga - S.C.D.O. Microcitemie e malattie rare ematologiche, Orbassano

10065

RECRUITING

Weill Cornell Med Coll-NYPH, New York

10461

ACTIVE_NOT_RECRUITING

Jacobi Medical Center, The Bronx

10467

NOT_YET_RECRUITING

Montefiore Medical Center, The Bronx

11203

RECRUITING

NYC Health+Hospitals, Brooklyn

11527

RECRUITING

Hippokration Hospital, Athens

11956

RECRUITING

Cairo University, Cairo, Egypt

12372

NOT_YET_RECRUITING

King Khalid University Hospital, Riyadh

13353

NOT_YET_RECRUITING

Charité - Campus Virchow-Klinikum - Klinik für Pädiatrie mit Schwerpunkt Onkologie und Hämatologie, Berlin

20010

NOT_YET_RECRUITING

Children's National Medical Center, Washington D.C.

20200

NOT_YET_RECRUITING

KEMRI-Walter-Reed Kericho, Kericho

21131

NOT_YET_RECRUITING

Alexandria University Hospital, Alexandria, Egypt

21211

RECRUITING

Chronic Care Center, Hazmiyeh

23298

NOT_YET_RECRUITING

Virginia Comm Univ Medical Ctr, Richmond

26504

RECRUITING

General University Hospital of Patras, Pátrai

27100

RECRUITING

Fondazione IRCCS Policlinico San Matteo, Pavia

27157

NOT_YET_RECRUITING

Atrium Health-Wake Forest Bapt, Winston-Salem

27705

RECRUITING

Duke University_Durham, Durham

27834

RECRUITING

East Carolina Univ-Greenville, Greenville

WITHDRAWN

East Carolina University_Greenville, Greenville

28046

RECRUITING

Hospital Universitario La Paz, Madrid

28204

NOT_YET_RECRUITING

Atrium Levine Children's/Atrium Health, Charlotte

29425

NOT_YET_RECRUITING

Medical University Of South Carolina_Charleston, Charleston

30303

RECRUITING

Emory University School of Medicine, Atlanta

30329

RECRUITING

Children's Healthcare Atlanta, Atlanta

30912

RECRUITING

Center for Blood Disorders Augusta University, Augusta

33023

RECRUITING

Foundation for Sickle Cell Disease Research, Hollywood

33110

NOT_YET_RECRUITING

Mersin University Medical Faculty Hospital, Hematology, Mersin

NOT_YET_RECRUITING

Mersin University Medical Faculty Pediatric Hematology, Mersin

33136

WITHDRAWN

Univ of Miami/SCCC, Miami

35128

RECRUITING

Azienda Ospedale Universita Padova, Padua

35233

ACTIVE_NOT_RECRUITING

Univ of Alabama Birmingham, Birmingham

38104

NOT_YET_RECRUITING

Methodist University Hospital, Memphis

40100

RECRUITING

Ahero Clinical Trials Unit, Kisumu, Kenya, Kisumu

NOT_YET_RECRUITING

KEMRI Kondele Children Hospital, Kisumu, Kisumu

41221

RECRUITING

General Hospital Of Larissa Koutlibaneio And Triantafylleio, Larissa

44519

NOT_YET_RECRUITING

Zagazig University Hospital, Alsharkia, Egypt

44720

ACTIVE_NOT_RECRUITING

Neuro-Behavioral Clinical Research, North Canton

45229

ACTIVE_NOT_RECRUITING

Cincinnati Child's Hsp Med Ctr, Cincinnati

48903

ACTIVE_NOT_RECRUITING

Hospital Universitario de Cruces, Barakaldo

53226

NOT_YET_RECRUITING

Versiti, CCBD_Milwaukee, Milwaukee

54642

NOT_YET_RECRUITING

'Ippokrateio' General Hospital of Thessaloniki, Thessaloniki

60612

NOT_YET_RECRUITING

Univer Of Illinois at Chicago, Chicago

63110

RECRUITING

Washington University-St.Louis, St Louis

69437

NOT_YET_RECRUITING

Hospices Civils de Lyon-Hopital Edouard Herriot, Lyon

70118

WITHDRAWN

Children's Hosp-New Orleans, New Orleans

75019

RECRUITING

Ap-Hp-Hopital Robert Debre, Paris

NOT_YET_RECRUITING

Ap-Hp-Hopital Robert Debre, Paris

77030

RECRUITING

Texas Children's Hospital_Houston, Houston

RECRUITING

UT Health University of Texas, Houston

79106

RECRUITING

Universitätsklinikum Freiburg - Kinder- und Jugendklinik, Freiburg im Breisgau

82943

NOT_YET_RECRUITING

Prince Mohammad Bin Naser Hospital, Jizan

85016

NOT_YET_RECRUITING

Phoenix Children's Hsptl, Phoenix

90027

ACTIVE_NOT_RECRUITING

Children's Hospital Los Angeles - Endocrinology, Los Angeles

RECRUITING

Children's Hospital Los Angeles - Endocrinology, Los Angeles

92868

WITHDRAWN

Children's Hosp Of Orange, Orange

RECRUITING

University Of California Irvine, Orange

94000

NOT_YET_RECRUITING

Ap-Hp-Hopital Henri Mondor, Créteil

94609

ACTIVE_NOT_RECRUITING

UCSF Oakland Benioff ChildHosp, Oakland

RECRUITING

UCSF Oakland Benioff ChildHosp, Oakland

98405

ACTIVE_NOT_RECRUITING

Mary Bridge Children's Health, Tacoma

102215

NOT_YET_RECRUITING

Lagos University Teaching Hospital, Lagos, Lagos

110029

NOT_YET_RECRUITING

All India Institute of Medical Sciences_Delhi, New Delhi

395002

NOT_YET_RECRUITING

Nirmal Hospital Pvt. Ltd., Gujarat

400022

NOT_YET_RECRUITING

K.J Somaiya Hospital and Research Centre, Mumbai

440012

NOT_YET_RECRUITING

Suretech Hospital and Research Centre Ltd., Maharashtra

492099

NOT_YET_RECRUITING

All India Institute of Medical Sciences (AIIMS), Raipur, Raipur

560002

NOT_YET_RECRUITING

Victoria Hospital, Bangalore, Bangalore

800212

NOT_YET_RECRUITING

Barau Dikko Teaching Hospital, Kaduna, Kaduna

4241317

RECRUITING

Abu El-Reesh El-Mounira Children University Hospital, Cairo, Egypt

06030

ACTIVE_NOT_RECRUITING

University of Connecticut, Farmington

02118

ACTIVE_NOT_RECRUITING

Boston Medical Center, Boston

V6Z1Y6

RECRUITING

St Pauls Hospital, Vancouver

M5G 1X8

ACTIVE_NOT_RECRUITING

The Hospital for Sick Children, Toronto

M5G 2C4

RECRUITING

University Health Network - Toronto General Hospital, Toronto

H3T 1C5

RECRUITING

CHU Ste-Justine, Montreal

00000

NOT_YET_RECRUITING

Gertrude's Children's Hospital, Nairobi, Nairobi

NOT_YET_RECRUITING

University of Nigeria Teaching Hospital, Enugu, Enugu

0000

NOT_YET_RECRUITING

KEMRI Siaya Clinical Research Annex Siaya County Referral Hospital, Siaya, Siaya

NOT_YET_RECRUITING

University College Hospital Paediatric Haematology and Oncology Unit, Ibadan, Ibadan

Unknown

RECRUITING

American University of Beirut Medical Centre, Hamra

08035

RECRUITING

Hospital Vall d'Hebron, Barcelona

01250

NOT_YET_RECRUITING

Baskent Universitesi Adana, Adana

06230

NOT_YET_RECRUITING

Hacettepe University Hematology, Ankara

SE1 9RT

NOT_YET_RECRUITING

Guy's Hospital, London

SE5 9RS

RECRUITING

Kings College Hospital, London

NOT_YET_RECRUITING

Kings College Hospital, London

W12 0NN

RECRUITING

Imperial College London, London

M13 9WL

RECRUITING

Manchester Royal Infirmary_Manchester_0, Manchester

S10 2JF

RECRUITING

Royal Hallamshire Hospital, Sheffield

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Novo Nordisk A/S

INDUSTRY