58
Participants
Start Date
January 16, 2025
Primary Completion Date
May 15, 2026
Study Completion Date
May 15, 2026
Nusinersen
Administered as specified in the treatment arm.
ThecaFlex DRx System
Implanted as specified in the treatment arm.
NOT_YET_RECRUITING
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma
RECRUITING
Children's Hospital of Philadelphia, Philadelphia
RECRUITING
Fondazione Serena Onlus - Centro Clinico Nemo_Milano, Milan
RECRUITING
Stacey Hall Developmental Pediatrics, Charlottesville
RECRUITING
Children's Hospital of the King's Daughters_Norfolk, Norfolk
RECRUITING
Hospital Universitario La Paz, Madrid
RECRUITING
Universitaetsklinikum Essen, Essen
RECRUITING
Hospital Universitari i Politecnic La Fe_Valencia, Valencia
RECRUITING
Helen DeVos Children's Hospita, Grand Rapids
RECRUITING
Texas Childrens Hospital Houston, Houston
RECRUITING
Hôpital Raymond Poincaré, Garches
RECRUITING
Children's Hospital of Orange County, Orange
RECRUITING
"Stanford University Medical Center , Department of Neurology_Palo Alto"
RECRUITING
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
RECRUITING
Boston Children's Hospital, Boston
RECRUITING
"Milton S. Hershey Medical Center , Pennsylvania State University_Hershey"
RECRUITING
Szpital Specjalistyczny im. L.Rydygiera w Krakowie, Krakow
RECRUITING
Instytut Centrum Zdrowia Matki Polki, Lodz
Lead Sponsor
Collaborators (1)
Alcyone Therapeutics, Inc
INDUSTRY
Biogen
INDUSTRY