Phase 2 Open-label Extension Study of AOC 1020 in Participants with Facioscapulohumeral Muscular Dystrophy (FSHD)

PHASE2Enrolling by invitationINTERVENTIONAL
Enrollment

84

Participants

Timeline

Start Date

July 25, 2024

Primary Completion Date

April 30, 2028

Study Completion Date

April 30, 2028

Conditions
FSHDFSHD1FSHD2FMDFMD2Fascioscapulohumeral Muscular DystrophyFascioscapulohumeral Muscular Dystrophy Type 1Fascioscapulohumeral Muscular Dystrophy Type 2Dystrophies, Facioscapulohumeral MuscularDystrophy, Facioscapulohumeral MuscularFacioscapulohumeral Muscular Dystrophy 1Facioscapulohumeral Muscular Dystrophy 2Facio-Scapulo-Humeral DystrophyAtrophy, FacioscapulohumeralAtrophies, FacioscapulohumeralFacioscapulohumeral AtrophyMuscular DystrophiesMuscular Dystrophy, FacioscapulohumeralFSH Muscular DystrophyLandouzy Dejerine DystrophyLandouzy-Dejerine Muscular DystrophyDystrophies, Landouzy-DejerineDystrophy, Landouzy-DejerineLandouzy-Dejerine SyndromeMuscular Dystrophy, Landouzy DejerineProgressive Muscular DystrophyFSH
Interventions
DRUG

AOC 1020

AOC 1020 will be administered via intravenous (IV) infusion

Trial Locations (17)

14642

University of Rochester Medical Center, Rochester

19104

University of Pennsylvania, Philadelphia

23298

Virginia Commonwealth University, Richmond

27708

Duke University, Durham

30329

Rare Disease Research, Atlanta

32608

University of Florida, Gainesville

43221

Ohio State University, Columbus

66205

Kansas University Medical Center, Kansas City

75390

University of Texas Southwestern, Dallas

80045

University of Colorado, Denver

90095

University of California Los Angeles, Los Angeles

92093

University of California San Diego, San Diego

94304

Stanford University, Palo Alto

98104

University of Washington, Seattle

K1Y 4E9

University of Ottawa, Ottawa

WIT 7HA

University College London, London

S10 2TN

University of Sheffield, Sheffield

Sponsors
All Listed Sponsors
lead

Avidity Biosciences, Inc.

INDUSTRY