FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases

RecruitingOBSERVATIONAL
Enrollment

1,000

Participants

Timeline

Start Date

June 10, 2024

Primary Completion Date

June 10, 2026

Study Completion Date

June 10, 2026

Conditions
Alpha-ThalassemiaBeta-ThalassemiaAmyloidosisAmyotrophic Lateral SclerosisCreutzfeld-Jakob DiseaseCystic FibrosisDuchenne Muscular DystrophyEarly-Onset Alzheimer DiseaseEhlers-Danlos SyndromeHuntington DiseaseGaucher DiseaseGM1 GangliosidosisMyasthenia GravisPompe DiseaseSickle Cell DiseaseTransthyretin Amyloid CardiomyopathyRare Diseases
Trial Locations (1)

94022

RECRUITING

xCures, Los Altos

Sponsors

Lead Sponsor

All Listed Sponsors
lead

xCures

INDUSTRY