Clinical Study of LY-M001 Injection in the Treatment of Adolescents With Type I Gaucher Disease

EARLY_PHASE1RecruitingINTERVENTIONAL
Enrollment

9

Participants

Timeline

Start Date

August 1, 2024

Primary Completion Date

August 31, 2025

Study Completion Date

August 31, 2029

Conditions
Gaucher Disease
Interventions
GENETIC

LY-M001

LY-M001 Injection by Single Intravenous Infusion

Trial Locations (1)

Unknown

RECRUITING

Shanghai Children's Medical Center, School of Medicine, Shanghai Jiao Tong University, Shanghai

All Listed Sponsors
lead

Shanghai Jiao Tong University School of Medicine

OTHER