Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy

RecruitingOBSERVATIONAL
Enrollment

44

Participants

Timeline

Start Date

May 12, 2025

Primary Completion Date

September 30, 2028

Study Completion Date

September 30, 2028

Conditions
LAMA2-MD \(Merosin Deficient Congenital Muscular Dystrophy, MDC1A\)
Trial Locations (14)

14627

RECRUITING

University of Rochester, Rochester

15224

NOT_YET_RECRUITING

Children's Hospital of Pittsburgh, Pittsburgh

20892

NOT_YET_RECRUITING

National Institute of Neurological Disorders and Stroke, NIH, Bethesda

43205

RECRUITING

Nationwide Children's Hospital, Columbus

45229

RECRUITING

Cincinnati Children's Hospital Medical Center, Cincinnati

52242

RECRUITING

University of Iowa Stead Family Children's Hospital, Iowa City

55108

RECRUITING

University of Minnesota, Saint Paul

60611

RECRUITING

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

63130

RECRUITING

Washington University in St. Louis, St Louis

75235

RECRUITING

University of Texas Southwestern, Dallas

84112

NOT_YET_RECRUITING

University of Utah, Salt Lake City

90095

RECRUITING

University of California, Los Angeles, Los Angeles

94305

RECRUITING

Stanford University, Stanford

02115

RECRUITING

Boston Children's Hospital, Boston

All Listed Sponsors
collaborator

National Institute of Neurological Disorders and Stroke (NINDS)

NIH

collaborator

Ann & Robert H Lurie Children's Hospital of Chicago

OTHER

collaborator

Children's Hospital Medical Center, Cincinnati

OTHER

collaborator

University of Iowa

OTHER

collaborator

Washington University School of Medicine

OTHER

collaborator

Stanford University

OTHER

collaborator

University of Utah

OTHER

collaborator

University of Rochester

OTHER

collaborator

University of Pittsburgh

OTHER

collaborator

University of Texas, Southwestern Medical Center at Dallas

OTHER

collaborator

University of Minnesota

OTHER

collaborator

University of California, Los Angeles

OTHER

collaborator

Boston Children's Hospital

OTHER

lead

Nationwide Children's Hospital

OTHER