Global Study of Del-desiran for the Treatment of DM1

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

159

Participants

Timeline

Start Date

May 30, 2024

Primary Completion Date

March 31, 2026

Study Completion Date

September 30, 2026

Conditions
DM1Myotonic DystrophyMyotonic Dystrophy 1MyotoniaMyotonic Dystrophy Type 1 (DM1)Dystrophy MyotonicMyotonic DisordersSteinert DiseaseSteinertMyotonic Muscular Dystrophy
Interventions
DRUG

AOC 1001 (del-desiran)

Del-desiran will be administered by intravenous (IV) infusion.

DRUG

Placebo

Placebo will be administered by intravenous (IV) infusion.

Trial Locations (34)

2100

Rigshospitalet, Copenhagen

8200

Aarhus University Hospital, Aarhus N

14642

University of Rochester Medical Center, Rochester

19104

University of Pennsylvania, Philadelphia

20014

Hospital Universitario Donostia, Donostia / San Sebastian

20162

Fondazione Serena Onlus - Centro Clinico NeMO Milano, Milan

21205

Kennedy Krieger Institute, Baltimore

23298

Virginia Commonwealth University, Richmond

27157

Wake Forest, Winston-Salem

27708

Duke University Medical Center, Durham

32608

University of Florida, Gainesville

33612

University Research Center of South Florida, Tampa

43221

Ohio State University, Columbus

45219

University of Cincinnati Gardner Neuroscience Institute, Cincinnati

46202

Indiana University (IU), Indianapolis

55455

University of Minnesota, Minneapolis

66205

Kansas University Medical Center, Kansas City

75013

AP-HP Hopital Pitie-Salpetriere, Paris

77030

Houston Methodist Neurological Institute, Houston

80045

University of Colorado, Denver

80336

Klinikum der Ludwig-Maximilians-Universitaet Muenchen, Munich

94305

Stanford University, Stanford

98104

University of Washington, Seattle

02215

Beth Israel Deaconess Medical Center, Boston

K1Y 4E9

The Ottawa Hospital, Ottawa

H3A 2B4

Montreal Neurological Institute, Montreal

038-1331

Aomori Hospital, Aomori

560-8552

National Hospital Organization Osaka Toneyama Medical Center, Osaka

565-0871

Osaka University Hospital, Osaka

187-8551

National Center of Neurology and Psychiatry, Tokyo

6229 HX

Maastricht University Medical Center, Maastricht

6525 GA

Stichting Radboud Universitair Medisch Centrum, Nijmegen

NW1 2BU

University College London Hospital, London

SW17 0QT

St. Georges University Hospitals NHS Foundation Trust, London

Sponsors
All Listed Sponsors
lead

Avidity Biosciences, Inc.

INDUSTRY