WiTNNess - TNNT1 Myopathy Natural History Study

RecruitingOBSERVATIONAL
Enrollment

40

Participants

Timeline

Start Date

September 23, 2018

Primary Completion Date

January 1, 2027

Study Completion Date

June 1, 2027

Conditions
TNNT1-associated MyopathyInfantile-onset Nemaline Rod MyopathyMyopathies, NemalineMyopathyMyopathy, RodMyopathy; HereditaryAmish Nemaline MyopathyNemaline Myopathy 5NEM5Genetic Muscle DiseaseRecessive Hereditary Disorder (Autosomal)ANM
Trial Locations (1)

17529

RECRUITING

Clinic for Special Children, Gordonville

All Listed Sponsors
lead

Clinic for Special Children

OTHER