phenotypeS in Non Ambulant Duchenne Muscular Dystrophy

RecruitingOBSERVATIONAL
Enrollment

250

Participants

Timeline

Start Date

August 30, 2022

Primary Completion Date

September 30, 2024

Study Completion Date

December 30, 2025

Conditions
Duchenne Muscular DystrophyNatural HistoryMotor Function; Retardation
Interventions
OTHER

Different Phenotypes of non ambulant patients with Duchenne Muscular Dystrophy

clinical and functional data collection of non ambulant patients with Duchenne muscular dystrophy

Trial Locations (2)

23842

RECRUITING

"IRCCS Eugenio Medea - Ass. La Nostra Famiglia", Bosisio Parini

Unknown

RECRUITING

Fondazione Policlinico Universitario A. Gemelli IRCCS, Roma

All Listed Sponsors
lead

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

OTHER