A Long-Term Follow-Up Study of Participants With Sickle Cell Disease or Transfusion Dependent β-Thalassemia Who Received EDIT-301

Enrolling by invitationOBSERVATIONAL
Enrollment

54

Participants

Timeline

Start Date

June 17, 2024

Primary Completion Date

August 31, 2040

Study Completion Date

August 31, 2040

Conditions
Sickle Cell DiseaseTransfusion-dependent Beta-ThalassemiaHemoglobinopathies
Interventions
OTHER

Safety and efficacy assessments

Assessed throughout the duration of the study.

Trial Locations (18)

10032

Columbia University Medical Center - Department of Pediatrics, New York

Columbia University Medical Center, New York

19104

Children's Hospital of Philadelphia, Philadelphia

28204

Atrium Health, Charlotte

29425

Medical University of South Carolina, Charleston

30322

Children's Healthcare of Atlanta, Atlanta

33701

Johns Hopkins All Children's Hospital, St. Petersburg

37203

Tristar Medical Group Children's Specialists/Sarah Cannon Center for Blood Cancers, Nashville

43205

Nationwide Children's Hospital, Columbus

44195

Cleveland Clinic, Cleveland

55410

University of Minnesota, Minneapolis

75246

Texas Oncology - Baylor Charles A. Sammons Cancer Center, Dallas

76104

Cook Children's, Fort Worth

80045

Children's Hospital Colorado, Aurora

94609

UCSF Benioff Children's Hospital, Oakland

06511

Smilow Cancer Hospital, New Haven

K1H 8L6

Ottawa Hospital Research Institute, Ottawa

M5G 2M9

Princess Margaret Cancer Centre-University Health Network, Toronto

Sponsors
All Listed Sponsors
lead

Editas Medicine, Inc.

INDUSTRY