Effect of Large Neutral Amino Acids in Adults With Classical Phenylketonuria

NARecruitingINTERVENTIONAL
Enrollment

30

Participants

Timeline

Start Date

November 1, 2024

Primary Completion Date

September 30, 2026

Study Completion Date

September 30, 2026

Conditions
Brain DiseasesBrain Diseases, MetabolicBrain Diseases, Metabolic, InbornGenetic Diseases, InbornMetabolism, Inborn ErrorsAmino Acid Metabolism, Inborn ErrorsMetabolic DiseasePhenylketonurias
Interventions
OTHER

PreKUnil® LNAA Medical Food for PKU

PreKUnil® LNAA Medical Food for PKU is a commercially available active LNAA treatment product for PKU.

Trial Locations (2)

2300

RECRUITING

Center for Inherited Metabolic Diseases, Copenhagen

Unknown

NOT_YET_RECRUITING

Copenhagen University Hospital, Rigshospitalet, Copenhagen

All Listed Sponsors
collaborator

Prekulab Ltd ApS

UNKNOWN

lead

Rigshospitalet, Denmark

OTHER