AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

January 10, 2025

Primary Completion Date

December 30, 2030

Study Completion Date

December 30, 2030

Conditions
Phenylketonurias
Interventions
GENETIC

NGGT002

adeno-associated viral vector with human phenylalanine hydroxylase gene

Trial Locations (4)

15224

RECRUITING

University of Pittsburgh Medical Center, Pittsburgh

55454

RECRUITING

University of Minnesota, Minneapolis

75390

RECRUITING

University or Texas, Southwestern medical Center, Dallas

07960

RECRUITING

Atlantic Health System, Morristown

All Listed Sponsors
lead

NGGT INC.

INDUSTRY