Understanding, Diagnosis and Monitoring of Thyroid Hormone Action Defects

RecruitingOBSERVATIONAL
Enrollment

150

Participants

Timeline

Start Date

January 1, 2023

Primary Completion Date

October 31, 2025

Study Completion Date

January 31, 2026

Conditions
Resistance, Thyroid Hormone
Interventions
GENETIC

NGS sequencing

analysis of candidate genes for RTHs syndromes, transporters defects or gene involved in thyroid hormone metabolism. Whole exome sequencing (WES) in a minority of cases

DIAGNOSTIC_TEST

serological tests

assessment of T4, T3 and other TH metabolites (LC-MS) in serum and dried blood spots

Trial Locations (2)

20145

RECRUITING

Istituto Auxologico Italiano IRCCS, Milan

Unknown

RECRUITING

Department of Endocrine & Metabolic Diseases, San Luca Hospital, Milan

All Listed Sponsors
collaborator

ASST Fatebenefratelli Sacco

OTHER

collaborator

Federico II University

OTHER

lead

Istituto Auxologico Italiano

OTHER