Study of ATX-01 in Participants With DM1

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

56

Participants

Timeline

Start Date

October 15, 2024

Primary Completion Date

June 30, 2026

Study Completion Date

June 30, 2026

Conditions
Myotonic Dystrophy 1
Interventions
DRUG

ATX-01

Solution for infusion

DRUG

Placebo

Solution for infusion

Trial Locations (9)

20014

RECRUITING

Hospital Universitario Donostia, Donostia / San Sebastian

20162

RECRUITING

The NeMO Clinical Center in Milan, Neurorehabilitation Unit, University of Milan, Milan

23298

RECRUITING

Virginia Commonwealth University, Richmond

32610

RECRUITING

University of Florida, Gainesville

66205

RECRUITING

University of Kansas Medical Center, Department of Neurology, Fairway

75651

RECRUITING

Institute of Myology, Paris

G7H 5H6

RECRUITING

Centre Intégré Universitaire de Santé et Services Sociaux du Saguenay-Lac-St-Jean, Chicoutimi

00168

RECRUITING

Fondazione Policlinico A. Gemelli- IRCCS, Rome

SW17 0RE

RECRUITING

St. George's University Hospital, London

Sponsors
All Listed Sponsors
lead

ARTHEx Biotech S.L.

INDUSTRY