A Natural History Study of RYR1-Related Disorders

RecruitingOBSERVATIONAL
Enrollment

150

Participants

Timeline

Start Date

March 11, 2025

Primary Completion Date

April 30, 2031

Study Completion Date

December 30, 2031

Conditions
Ryanodine Receptor 1-Related MyopathyRyanodine Receptor 1 Related Disorders
Trial Locations (1)

20892

RECRUITING

National Institutes of Health Clinical Center, Bethesda

All Listed Sponsors
lead

National Institutes of Health Clinical Center (CC)

NIH