Long-Term Follow-Up (LTFU) for Gene Therapy of Leukocyte Adhesion Deficiency-I (LAD-I)

Enrolling by invitationOBSERVATIONAL
Enrollment

9

Participants

Timeline

Start Date

March 9, 2022

Primary Completion Date

March 31, 2037

Study Completion Date

March 31, 2037

Conditions
Leukocyte Adhesion Deficiency
Trial Locations (3)

28009

Hospital Infantil Universitario Niño Jesús, Madrid

90095-1489

University of California, Los Angeles (UCLA), Los Angeles

WC1N 1EH

University College London Great Ormond Street Institute of Child Health (GOSH), London

All Listed Sponsors
lead

Rocket Pharmaceuticals Inc.

INDUSTRY