A Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in HT-1 Patients

RecruitingOBSERVATIONAL
Enrollment

15

Participants

Timeline

Start Date

September 30, 2025

Primary Completion Date

June 30, 2027

Study Completion Date

June 30, 2027

Conditions
Hereditary Tyrosinemia, Type I
Interventions
DRUG

Nitisinone

According to prescription

Trial Locations (4)

Unknown

NOT_YET_RECRUITING

Swedish Orphan Biovitrum Research Site, Beijing

NOT_YET_RECRUITING

Swedish Orphan Biovitrum Research Site, Chongqing

RECRUITING

Swedish Orphan Biovitrum Research Site, Hefei

RECRUITING

Swedish Orphan Biovitrum Research Site, Wuhan

Sponsors
All Listed Sponsors
lead

Swedish Orphan Biovitrum

INDUSTRY

NCT06227429 - A Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in HT-1 Patients | Biotech Hunter | Biotech Hunter