A Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in HT-1 Patients

RecruitingOBSERVATIONAL
Enrollment

15

Participants

Timeline

Start Date

September 30, 2025

Primary Completion Date

June 30, 2027

Study Completion Date

June 30, 2027

Conditions
Hereditary Tyrosinemia, Type I
Interventions
DRUG

Nitisinone

According to prescription

Trial Locations (4)

Unknown

NOT_YET_RECRUITING

Swedish Orphan Biovitrum Research Site, Beijing

NOT_YET_RECRUITING

Swedish Orphan Biovitrum Research Site, Chongqing

RECRUITING

Swedish Orphan Biovitrum Research Site, Hefei

RECRUITING

Swedish Orphan Biovitrum Research Site, Wuhan

Sponsors
All Listed Sponsors
lead

Swedish Orphan Biovitrum

INDUSTRY