Danon Disease Natural History Study

RecruitingOBSERVATIONAL
Enrollment

46

Participants

Timeline

Start Date

December 20, 2023

Primary Completion Date

August 31, 2026

Study Completion Date

August 31, 2026

Conditions
Danon Disease
Interventions
OTHER

No intervention

No intervention

Trial Locations (13)

10032

RECRUITING

Columbia University Medical Center/New York Presbyterian, New York

32610

RECRUITING

University of Florida College of Medicine, Gainesville

48109

RECRUITING

University of Michigan, Ann Arbor

50139

RECRUITING

Azienda Ospedaliero Universitaria, Florence

63110

RECRUITING

Washington University, St Louis

77030

RECRUITING

Texas Children's Hospital, Houston

80045

RECRUITING

Children's Hospital Colorado, Aurora

85016

RECRUITING

Phoenix Children's Hospital, Phoenix

92037

RECRUITING

University of California, San Diego, La Jolla

5265601

RECRUITING

Sheba Medical Center, Ramat Gan

Unknown

RECRUITING

German Heart Center Munich, München

RECRUITING

Hospital Universitario Puerta de Hierro Majadahonda, Majadahonda

WC1N 1DZ

RECRUITING

University College London - Great Ormond Street Institute of Child Health, London

All Listed Sponsors
lead

Rocket Pharmaceuticals Inc.

INDUSTRY