400
Participants
Start Date
November 27, 2023
Primary Completion Date
December 31, 2043
Study Completion Date
December 31, 2043
RECRUITING
Royal Children's Hospital Melbourne, Parkville
RECRUITING
Mount Sinai Kravis Children's Hospital, New York
RECRUITING
Nemours Alfred I. Dupont Hospital for Children, Wilmington
RECRUITING
Children's National Health System, Washington D.C.
NOT_YET_RECRUITING
The Johns Hopkins University School of Medicine, Baltimore
NOT_YET_RECRUITING
Nationwide Children's Hospital, Columbus
NOT_YET_RECRUITING
Akron Children's Hospital, Akron
RECRUITING
Medical College of Wisconsin, Children's Hospital, Milwaukee
RECRUITING
University of Minnesota Masonic Children's Hospital, Minneapolis
RECRUITING
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
RECRUITING
Washington University School of Medicine in St. Louis, St Louis
RECRUITING
University of Missouri, Columbia
RECRUITING
Cook Children's Endocrinology, Fort Worth
RECRUITING
Phoenix Children's Hospital, Phoenix
NOT_YET_RECRUITING
Cedars-Sinai Medical Center, Los Angeles
RECRUITING
UCSF Benioff Children's Hospital, Oakland
RECRUITING
Boston Children's Hospital, Boston
NOT_YET_RECRUITING
Hospital de Pediatria SAMIC Prof. Dr. Juan P Garrahan, Buenos Aires
NOT_YET_RECRUITING
Hospital de Clinicas de Porto Algre, Porto Alegre
NOT_YET_RECRUITING
Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto, Ribeirão Preto
RECRUITING
Stollery Children's Hospital, Edmonton
RECRUITING
SickKids - The Hospital for Sick Children, Toronto
NOT_YET_RECRUITING
Centre Hospitalier Universitaire Sainte-Justine, Montreal
RECRUITING
Hospices Civils de Lyon - Hôpital Femme Mère Enfant, Lyon
RECRUITING
Hopital de la Timone, Marseille
RECRUITING
Hôpital Necker-Enfants Malades, Paris
RECRUITING
CHU de Toulouse - Hopital des Efants, Toulouse
RECRUITING
Uniklinik Koln, Cologne
RECRUITING
Universitatskinderklinik Magdeburg, Magdeburg
RECRUITING
Istituto Giannina Gaslini, Genoa
NOT_YET_RECRUITING
Ospedale Pediatrico Bambino Gesù, Roma
RECRUITING
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan
RECRUITING
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome
RECRUITING
Kumamoto University Hospital, Kumamoto
RECRUITING
Osaka University Hospital, Suita
RECRUITING
Tottori University Hospital, Yonago
NOT_YET_RECRUITING
Tokushima University Hospital, Tokushima
RECRUITING
Institute of Science Tokyo Hospital, Tokyo
RECRUITING
Hospital Universitario La Paz, Madrid
RECRUITING
Vithas Hospital San Jose, Vitoria-Gasteiz
RECRUITING
Great Ormond Street Hospital for Children NHS Foundation Trust, London
NOT_YET_RECRUITING
Myriad Trials Ltd, London
RECRUITING
NHS Greater Glasgow and Clyde, Glasgow
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY