Low Dose Treosulfan Based Conditioning Regimen and PTCy in HSCT for Nijmegen Breakage Syndrome

PHASE2RecruitingINTERVENTIONAL
Enrollment

10

Participants

Timeline

Start Date

November 22, 2023

Primary Completion Date

January 31, 2027

Study Completion Date

January 31, 2029

Conditions
Nijmegen Breakage Syndrome
Interventions
DRUG

Treosulfan

Treosulfan 21mg/m2 (days -6, -5, -4)

Trial Locations (1)

Unknown

RECRUITING

HSCT department, Moscow

All Listed Sponsors
lead

Federal Research Institute of Pediatric Hematology, Oncology and Immunology

OTHER