Real-World Use of Novel Treatments in Patients With Spinal Muscular Atrophy (SMA): A Multi-Site Retrospective Chart Review of Pediatric SMA Patients Outside of the United States

CompletedOBSERVATIONAL
Enrollment

162

Participants

Timeline

Start Date

May 5, 2022

Primary Completion Date

December 30, 2022

Study Completion Date

December 30, 2022

Conditions
Spinal Muscular Atrophy
Trial Locations (1)

60015

Novartis, Bannockburn

Sponsors
All Listed Sponsors
lead

Novartis Pharmaceuticals

INDUSTRY