Study to Learn About the Safety of Fazirsiran and if it Can Help People With Alpha-1 Antitrypsin Liver Disease With Mild Liver Scarring (Fibrosis)

PHASE3RecruitingINTERVENTIONAL
Enrollment

50

Participants

Timeline

Start Date

March 1, 2024

Primary Completion Date

August 26, 2028

Study Completion Date

August 26, 2028

Conditions
Alpha1-Antitrypsin Deficiency
Interventions
DRUG

Fazirsiran Injection

Fazirsiran will be injected subcutaneously.

DRUG

Placebo

Fazirsiran matching placebo.

Trial Locations (39)

2650

RECRUITING

UZ Antwerpen, Antwerp

3000

RECRUITING

UZ Leuven, Leuven

3010

RECRUITING

Universitätsspital Bern, Bern

8036

RECRUITING

LKH-Universitätsklinikum Graz, Graz

9020

RECRUITING

KABEG - Klinikum Klagenfurt Am Wörthersee, Klagenfurt

13353

RECRUITING

Charité - Campus Virchow-Klinikum, Berlin

14186

RECRUITING

Karolinska Universitetssjukhuset Huddinge, Huddinge

27100

RECRUITING

Fondazione IRCCS Policlinico San Matteo, Pavia

30625

RECRUITING

Hannover Medical School, Hanover

33136

RECRUITING

Schiff Center for Liver Diseases/University of Miami, Miami

35000

RECRUITING

Hopital PONTCHAILLOU CHU de Rennes, Rennes

41018

RECRUITING

Hospital Universitario Virgen del Rocio - PPDS, Seville

48109

RECRUITING

University of Michigan Hospital - 1500 E Medical Center Dr, Ann Arbor

52074

RECRUITING

Universitätsklinikum der RWTH Aachen, Aachen

69317

RECRUITING

Hôpital de La Croix Rousse, Lyon

72076

RECRUITING

Universitätsklinikum Tübingen, Tübingen

78215

RECRUITING

Texas Liver Institute American Research Corporation, San Antonio

80907

RECRUITING

Peak Gastroenterology Associates, Colorado Springs

94800

RECRUITING

Hôpital Paul Brousse, Val-de-Marne

85013-4224

RECRUITING

St Joseph's Hospital and Medical Center, Phoenix

85054-4502

RECRUITING

Mayo Clinic - PPDS, Phoenix

85724-0001

RECRUITING

University of Arizona Thomas D. Boyer Liver Institute, Tucson

90095-3075

RECRUITING

UCLA Pulmonary and Critical Care, Los Angeles

94143-2203

RECRUITING

University of California Benioff Children's Hospital, San Francisco

46202-2266

RECRUITING

Indiana University School of Medicine-Indianapolis, Indianapolis

52242-1009

RECRUITING

University Of Iowa Hospitals And Clinics, Iowa City

02118-2335

RECRUITING

Boston Medical Center, Boston

48377-3600

RECRUITING

Henry Ford Health System, Novi

10016-6402

RECRUITING

NYU Langone Medical Center, New York

10032-3722

RECRUITING

Columbia University Irving Medical Center, New York

44106-1716

RECRUITING

University Hospitals Cleveland Medical Center, Cleveland

17033-2360

RECRUITING

Penn State Health Milton S. Hershey Medical Center, Hershey

23602-4414

RECRUITING

Bon Secours St. Mary's Hospital, Newport

M5T 3A9

RECRUITING

Inspiration Research Limited, Toronto

41-400

RECRUITING

ID Clinic Arkadiusz Pisula, Mysłowice

4710-243

RECRUITING

CCA Hospital Braga, Braga

9000-168

RECRUITING

Hospital Dr. Nélio Mendonça, Funchal

4099-001

RECRUITING

Centro Hospitalar de Universitário de Santo António E.P.E, Porto

SE5 9RS

RECRUITING

King's College Hospital, London

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Takeda

INDUSTRY