A Prospective Natural History and Outcome Measure Discovery Study of Charcot-Marie-Tooth Disease, Type 4J

RecruitingOBSERVATIONAL
Enrollment

20

Participants

Timeline

Start Date

July 29, 2024

Primary Completion Date

March 1, 2027

Study Completion Date

March 1, 2028

Conditions
Peripheral NeuropathyNeuro-Degenerative DiseaseNeuromuscular Diseases
Trial Locations (3)

52242

RECRUITING

University of Iowa, Iowa City

75390

RECRUITING

University of Texas Southwestern, Dallas

94305

RECRUITING

Stanford University, San Francisco

Sponsors
All Listed Sponsors
lead

Elpida Therapeutics SPC

INDUSTRY