Study of ARO-DM1 in Subjects With Type 1 Myotonic Dystrophy

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

90

Participants

Timeline

Start Date

March 4, 2024

Primary Completion Date

September 30, 2026

Study Completion Date

September 30, 2026

Conditions
Myotonic Dystrophy 1
Interventions
DRUG

ARO-DM1 for Injection

single or multiple doses of ARO-DM1 by intravenous (IV) infusion

DRUG

Placebo

calculated volume to match active treatment by IV infusion

Trial Locations (11)

2170

RECRUITING

Research Site, Liverpool

3004

RECRUITING

Research Site, Melbourne

4029

RECRUITING

Research Site, Herston

4575

RECRUITING

Research Site, Birtinya

8011

RECRUITING

Research Site, Christchurch

10041

RECRUITING

Research Site, Taipei

10700

RECRUITING

Research Site, Bangkok

11217

RECRUITING

Research Site, Taipei

40447

RECRUITING

Research Site, Taichung

52000

RECRUITING

Research Site, Lampang

90110

RECRUITING

Research Site, Hat Yai

Sponsors
All Listed Sponsors
lead

Arrowhead Pharmaceuticals

INDUSTRY