A 5-year Natural History Study in LAMA2-related Muscular Dystrophy and SELENON-related Myopathy.

RecruitingOBSERVATIONAL
Enrollment

40

Participants

Timeline

Start Date

October 6, 2023

Primary Completion Date

September 1, 2026

Study Completion Date

September 1, 2026

Conditions
LAMA2-related Muscular DystrophySELENON-related Myopathy
Interventions
OTHER

No intervention

No intervention

Trial Locations (1)

6525GA

RECRUITING

Radboudumc, Nijmegen

All Listed Sponsors
lead

Radboud University Medical Center

OTHER