765
Participants
Start Date
December 13, 2023
Primary Completion Date
December 31, 2027
Study Completion Date
April 30, 2028
NTLA-2001
NTLA-2001 (55mg) by IV infusion
Placebo
Normal saline (0.9% NaCl) by IV infusion
RECRUITING
New York University (NYU) School of Medicine - Langone Medical Center, New York
RECRUITING
Columbia University Medical Center, New York
RECRUITING
Allegheny General Hospital, Pittsburgh
RECRUITING
University of Pittsburgh Medical Center, Pittsburgh
RECRUITING
Penn Presbyterian Medical Center, Philadelphia
RECRUITING
MedStar Washington Hospital Center - MedStar Heart and Vascular Institute, Washington D.C.
RECRUITING
Johns Hopkins University, Baltimore
RECRUITING
INOVA Fairfax Hospital, Falls Church
RECRUITING
Virginia Commonwealth University - Department of Internal Medicine, Richmond
RECRUITING
Duke University Medical Center, Durham
RECRUITING
Medical University of South Carolina, Charleston
RECRUITING
Emory University School of Medicine, Atlanta
RECRUITING
Mayo Clinic - Jacksonville, Jacksonville
RECRUITING
Cleveland Clinic of Florida, Weston
RECRUITING
University of Kentucky Gill Heart Institute, Lexington
RECRUITING
Ohio Health Research Institute, Columbus
RECRUITING
Cleveland Clinic, Cleveland
RECRUITING
Indiana University Health, Indianapolis
RECRUITING
University of Michigan, Ann Arbor
ACTIVE_NOT_RECRUITING
Barbara Ann Karmanos Cancer Institute, Detroit
RECRUITING
Mayo Clinic, Rochester
RECRUITING
Northwestern University, Chicago
RECRUITING
St. Luke's Hospital, Kansas City
RECRUITING
Baylor Scott and White - The Heart Hospital Baylor Plano, Plano
RECRUITING
Baylor Scott & White Research Institute, Dallas
RECRUITING
University of Texas Southwestern Medical Center, Dallas
RECRUITING
Baylor College of Medicine, Houston
RECRUITING
Houston Methodist Hospital, Houston
RECRUITING
University of Colorado Denver, Denver
RECRUITING
University of Arizona, Tucson
RECRUITING
Cedars-Sinai Medical Center, Los Angeles
RECRUITING
Western Greater Los Angeles VA Medical Center, Los Angeles
RECRUITING
University of California, San Diego (UCSD) - Medical Center, San Diego
RECRUITING
Stanford University, Palo Alto
RECRUITING
Oregon Health and Science University (OHSU), Portland
RECRUITING
Yale University School of Medicine, New Haven
RECRUITING
Brigham and Women's Hospital, Boston
RECRUITING
Boston University School of Medicine, Boston
RECRUITING
Fundacion Favalro, Buenos Aires
RECRUITING
Hospital Italiano de Buenos Aires, Buenos Aires
RECRUITING
ICBA, Buenos Aires
RECRUITING
Fundacion Favaloro, Ciudad Autonoma de Buenos Aire
RECRUITING
Hospital Italiano de Buenos Aires, Ciudad Autonoma de Buenos Aire
RECRUITING
Hospital Privado de Rosario, Rosario
RECRUITING
The Canberra Hospital, Garran
RECRUITING
Westmead Hospital, Westmead
ACTIVE_NOT_RECRUITING
Cairns Hospital, Cairns
RECRUITING
Eastern Health - Box Hill Hospital, Box Hill
RECRUITING
Fiona Stanley Hospital, Perth
RECRUITING
Royal Adelaide Hospital, Adelaide
RECRUITING
The Alfred Hospital, Melbourne
RECRUITING
Princess Alexandra Hospital, Woolloongabba
RECRUITING
Medizinische Universitaet Innsbruck, Innsbruck
RECRUITING
Universitaesklinikum St. Poelten, Sankt Pölten
RECRUITING
AZ Sint-Jan Brugge, Bruges
RECRUITING
Universite Libre de Bruxelles (ULB) - Hopital Erasme, Brussels
RECRUITING
Antwerp University Hospital, Edegem
RECRUITING
UZ Leuven, Leuven
RECRUITING
Centre Hospitalier Regional de la Citadelle, Liège
RECRUITING
Centro de Pesquisa NUPEC - Instituto Orizonti em Belo Horizonte, Belo Horizonte
RECRUITING
Complexo Hospitalar de Niterói (CHN-DASA), Niterói
RECRUITING
CAPED - Centro Avancado de Pesquisa, Ribeirão Preto
RECRUITING
HCFMRP - Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto, Ribeirão Preto
RECRUITING
Cardiopulmonar da Bahia S. A. (Hospital Cardio Pulmonar), Salvador
RECRUITING
Hospital Israelita Albert Einstein, São Paulo
RECRUITING
Instituto Dante Pazzanese de Cardiologia, São Paulo
RECRUITING
Instituto do Coracao (InCor) do Hospital das Clinicas da FMUSP, São Paulo
RECRUITING
PSEG Centro de Pesquisa Clinica S.A., São Paulo
RECRUITING
Alberta Health Services - University of Calgary, Calgary
RECRUITING
Vancouver Coastal Health Research Institute, Vancouver
RECRUITING
University Health Network - Toronto General Hospital, Toronto
RECRUITING
McGill University Health Centre, Montreal
RECRUITING
Fakultni nemocnice u sv. Anny v Brne, Brno
RECRUITING
Aarhus University Hospital, Aarhus
RECRUITING
Rigshospitalet, Copenhagen
RECRUITING
AP-HP Hopital Henri Mondor, Créteil
RECRUITING
AP-HM - Hopital de la Timone, Marseille
RECRUITING
AP-HP Hopital Bichat - Claude Bernard, Paris
RECRUITING
CHU Rennes - Hopital Pontchaillou, Rennes
RECRUITING
CHU de Toulouse - Hopital Rangueil, Toulouse
RECRUITING
Charite Universitaetsmedizin Berlin, Berlin
RECRUITING
Universitaetsklinikum Essen, Essen
RECRUITING
Universitaetsklinikum Heidelberg, Heidelberg
RECRUITING
Universitaetsklinikum Wuerzburg, Würzburg
RECRUITING
Semmelweis Egyetem Belgyogyaszati es Hematologiai Klinika, Budapest
RECRUITING
Rambam Health Care Campus, Haifa
RECRUITING
Hadassah University Hospital, Ein Karem, Jerusalem
RECRUITING
Sheba Medical Center, Tel Litwinsky
RECRUITING
IRCCS Azienda Ospedaliero-Universitaria di Bologna - Policlinico di Sant'Orsola, Bologna
RECRUITING
Azienda Ospedaliero-Universitaria di Ferrara-Arcispedale Sant'Anna, Cona
RECRUITING
Azienda Ospedaliero-Universitaria Careggi, Florence
RECRUITING
Ospedale Policlinico San Martino IRCCS, Genova
RECRUITING
Fondazione IRCCS Policlinico San Matteo, Pavia
RECRUITING
Fondazione Toscana Gabriele Monasterio per la Ricerca Medica, Pisa
RECRUITING
Azienda sanitaria universitaria Giuliano Isontina (ASU GI) - Ospedale di Cattinara, Trieste
RECRUITING
Kumamoto University Hospital, Kumamoto
RECRUITING
National Cerebral and Cardiovascular Center, Osaka
RECRUITING
The University of Tokyo Hospital, Tokyo
RECRUITING
Toyama University Hospital, Toyama
RECRUITING
Instituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran, Mexico City
RECRUITING
University Medical Center, Groningen
RECRUITING
Erasmus MC, Rotterdam
RECRUITING
Universitair Medisch Centrum Utrecht, Utrecht
RECRUITING
New Zealand Clinical Research, Auckland
RECRUITING
New Zealand Clinical Research, Christchurch
RECRUITING
Oslo University Hospital - Rikshospitalet, Oslo
RECRUITING
Centro Hospitalar Universitario de Lisboa Norte, Lisbon
RECRUITING
Centro Hospitalar Universitario do Porto, Porto
RECRUITING
National Heart Centre, Singapore
RECRUITING
National University Hospital, Singapore
RECRUITING
Chonnam National University Hospital, Gwangju
RECRUITING
Samsung Medical Center, Seoul
RECRUITING
Seoul National University Hospital, Seoul
RECRUITING
Severance Hospital, Yonsei University Health System, Seoul
RECRUITING
Hospital Universitario de A Coruna, A Coruña
RECRUITING
Hospital Universitari de Bellvitge, Barcelona
RECRUITING
Hospital Universitario Vall d'Hebron, Barcelona
RECRUITING
Hospital Universitario Puerta de Hierro, Majadahonda
RECRUITING
Hospital Universitario Virgen de la Victoria, Málaga
RECRUITING
Hospital Universitario Son Llatzer, Palma de Mallorca
RECRUITING
Karolinska University Hospital, Stockholm
RECRUITING
University Hospital of Umea, Umeå
RECRUITING
Far Eastern Memorial Hospital, New Taipei City
RECRUITING
National Taiwan University Hospital, Taipei
RECRUITING
Taipai Veterans General Hospital, Taipei
ACTIVE_NOT_RECRUITING
Synexus Midlands Clinical Research Centre, Birmingham
ACTIVE_NOT_RECRUITING
Synexus Wales Clinical Research Centre, Cardiff
ACTIVE_NOT_RECRUITING
Synexus Scotland Clinical Research Centre, Glasgow
ACTIVE_NOT_RECRUITING
Synexus Hexham Clinical Research Centre, Hexham
ACTIVE_NOT_RECRUITING
Synexus Merseyside Clinical Research Centre, Liverpool
RECRUITING
Richmond Pharmacology, London
ACTIVE_NOT_RECRUITING
Synexus Manchester Clinical Research Centre, Manchester
Lead Sponsor
Regeneron Pharmaceuticals
INDUSTRY
Intellia Therapeutics
INDUSTRY