NCT06019637View on ClinicalTrials.gov

A Long-term Safety Study in Brazilian Patients With a Diagnosis of Spinal Muscular Atrophy Treated With Zolgensma

RecruitingOBSERVATIONAL
Enrollment

50

Participants

Timeline

Start Date

November 22, 2023

Primary Completion Date

September 30, 2038

Study Completion Date

September 30, 2038

Conditions
Spinal Muscular Atrophies
Interventions
OTHER

Onasemnogene Abeparvovec

Retrospective and prospective observational study. There is no treatment allocation.

Trial Locations (2)

81520-060

RECRUITING

Novartis Investigative Site, Curitiba

05403-000

RECRUITING

Novartis Investigative Site, São Paulo

Sponsors
All Listed Sponsors
lead

Novartis Pharmaceuticals

INDUSTRY